Sma drug works after 4 years

Those arriving from Dallas are new, important confirmations of the efficacy and safety of the drug for Sma that helps the muscles function. In fact, during the Texan conference of the Muscular Dystrophy Association, long-term data were presented on risdiplam, a medicine that supports the production of the missing protein in people with spinal muscular atrophy (Sma) and which prevents the muscles from working as they should. .